Genome Editing And Gene Therapy For Genetic Diseases

2^nd World Congress on

Pharmaceutical Chemistry and Drug Development

October 09-10, 2025 | Philadelphia, USA

Philadelphia, USA

Email: pharmaceuticalchem@scitechconference.com
Phone: +44 2045874848
WhatsApp: +44 2045250803

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Genome Editing and Gene Therapy for Genetic Diseases

Genome Editing and Gene Therapy for Genetic Diseases

Genome editing and gene therapy have emerged as innovative technologies in the realm of medicine, offering promising solutions for treating genetic diseases. By precisely modifying DNA sequences, genome editing tools such as CRISPR-Cas9 hold the potential to correct faulty genes that underlie inherited disorders. This targeted approach not only allows for the correction of disease-causing mutations but also opens up avenues for personalized medicine tailored to individual patient's genetic makeup. On the other hand, gene therapy involves delivering functional genes into a patient's cells to replace or supplement defective ones, offering a promising treatment option for genetic diseases. While these technologies present exciting prospects, there are ethical considerations regarding their use and potential unforeseen consequences that must be considered in research and clinical applications. As advancements continue in this field, genome editing and gene therapy hold great promise for revolutionizing the treatment of genetic diseases and improving patient outcomes.